Mitochondrial disorders are complex conditions for which few treatments are available. Now, using microscopic worms, researchers at The Children’s Hospital of Philadelphia (CHOP), are researching if existing human drugs aimed at improving metabolism and restore shortened lifespans, can open the opportunity for human clinical trials on innovative therapies for these…
Sponsored Content
Recent Posts
- Porphyria treatment now approved in Canada to prevent sun skin damage
- Genetic testing reveals young woman’s porphyria after years of misdiagnosis
- New oral drug shows big promise in small trial as a porphyria treatment
- Safety study points to possible new side effect signals in AHP treatment
- The extraordinary people who make life better for the porphyria community
- Treatment with hemin delays dialysis, slows kidney decline in woman with AIP
- New AIP study finds higher rates of hypertension, heart changes
- Program provides early access to experimental EPP treatment
- Acute porphyria drug safety database now available in Spanish