• Porphyria Cutanea Tarda Solved by Treating HCV Infection, Study Reports
  • Global Rare Disease Group’s Focus: 1,000 New Therapies by 2027, Despite COVID-19
  • The Assistance Fund Launches Aid Program for Out-of-pocket Medical Costs
  • Pediatric Rare Disease Therapies Increase, But Most Repurposed, Study Finds
  • Givlaari Approved in EU for Patients With Acute Hepatic Porphyria
  • Video: BioNews’ Social Media Campaign Highlights #WhatMakesMeRare
  • Elsevier Opens Books, Review Articles to Rare Disease Researchers Starting Feb. 29
  • Advice on Starting Nonprofit Groups for Rare and Other Diseases Focus of NORD Webinar
  • Patients, Supporters Worldwide Recognizing Rare Disease Day 2020
  • AIP Patients Use Fewer Healthcare Resources When They Take Hemin as Preventive Therapy, US Study Reports
  • FDA Efforts to Bring Patients into Treatment Decisions Focus of NORD Webinar
  • With Post-Brexit Move to Amsterdam Complete, EMA Renews Rare Disease Focus