• Non-Gastrointestinal Symptoms in Crohn’s Patients Could Signal Acute Intermittent Porphyria, Case Report Suggests
  • Iron-Regulating Mechanism May Open Door to New Porphyria Therapies, Study Suggests
  • Porphyria Diagnosed After PRES Suspected in Teenager
  • Alnylam Selects PANTHERx to Distribute its Recently Approved AHP Treatment Givlaari
  • Gene Therapy Takes Center Stage at 2019 NORD Summit
  • HHS Secretary Alex Azar Touts White House Efforts to Cure Rare Diseases
  • Alnylam Calls for Applicants for ‘Advocacy for Impact’ Grants Helping Rare Disease Communities
  • Givosiran Approved by FDA for Treating Adults with Acute Hepatic Porphyria
  • Rare Disease Film Festival Highlights Patient and Researcher Unity
  • HMBS Mutations Linked to Acute Intermittent Porphyria May Vary According to Ethnicity, Study Suggests
  • Recurrent Attacks in AHP Patients Serious and Lead to Chronic Symptoms, Study Based on Natural History Finds
  • FDA Approves Scenesse to Increase Pain-Free Light Exposure for Adults with EPP