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March 12, 2020 News by Patricia Inácio, PhD

Pediatric Rare Disease Therapies Increase, But Most Repurposed, Study Finds

The number of treatments for children with rare diseases has grown over the past decade, according to a new study. However, despite the increase, nearly 7,000 rare diseases are still lacking treatment. And federal incentives to boost treatment development for these rare diseases have primarily focused not on creating new…

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